Search for Clinical Trial Results
Lysosomal Storage Diseases - 50 Studies Found
Status | Study |
Recruiting |
Study Name: Lysosomal Storage Disease: Health, Development, and Functional Outcome Surveillance in Preschool Children Condition:
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Not yet recruiting |
Study Name: Diet and Exercise in Pompe Disease Condition:
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Terminated |
Study Name: Intrathecal Enzyme Replacement Therapy for Spinal Cord Compression in Mucopolysaccharidosis (MPS) I Condition:
Interventions: Drug: laronidase 0.58 mg/ml solution for intravenous injection, dose 1.74 mg intrathecally once per mont |
Active, not recruiting |
Study Name: Characterization of the Patient Population With Galactosialidosis Condition: Galactosialidosis Date: 2011-08-11 |
Completed |
Study Name: Magnetic Stimulation of the Human Nervous System Condition:
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